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PACULit Literature Updates August 2025: Pediatrics Pediatrics AAV9-Mediated Gene Therapy for Infantile-Onset Pompes Disease

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PACULit Daily Literature Update: AAV9-Mediated Gene Therapy for Infantile-Onset Pompes Disease
PACULit Literature Updates August 2025: Pediatrics AAV9-Mediated Gene Therapy for Infantile-Onset Pompes Disease Quiz
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