PACULit Literature Updates August 2025: Pediatrics Pediatrics AAV9-Mediated Gene Therapy for Infantile-Onset Pompes Disease Lesson Content 0% Complete 0/1 Steps PACULit Daily Literature Update: AAV9-Mediated Gene Therapy for Infantile-Onset Pompes Disease PACULit Literature Updates August 2025: Pediatrics AAV9-Mediated Gene Therapy for Infantile-Onset Pompes Disease Quiz Previous Lesson Back to Course Next Lesson